Muscular Dystrophy

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Cardiac stem cell therapy may heal heart damage caused by Duchenne muscular dystrophy

ScienceDaily, Source: Cedars-Sinai Medical Center ~ November 18, 2014 Injections of cardiac stem cells might help reverse heart damage caused by Duchenne muscular dystrophy, potentially resulting in a longer life expectancy for patients with the chronic muscle-wasting disease, researchers report. Researchers at the Cedars-Sinai Heart Institute have found that injections of cardiac stem cells might

After FDA Approval, Duchenne’s Muscular Dystrophy Patient Receives First Umbilical Cord Stem Cell Treatment in the United States

Virtual-Strategy Magazine, Source: PR Webb ~ September 10, 2014 Ryan Benton, a 28 year-old Duchenne’s muscular dystrophy patient from Wichita, Kansas, received his first umbilical cord tissue-derived mesenchymal stem cell treatment yesterday at Asthma and Allergy Specialists of Wichita, KS following US FDA approval of his doctor’s application for a single patient, investigational new drug

Researchers trigger muscle repair in mice with muscular dystrophy

Medical News Today, by Honor Whiteman ~ September 8, 2014 For muscle-wasting disorders such as muscular dystrophy, there are currently no treatments to halt progression. But researchers from the Sanford-Burnham Medical Research Institute in La Jolla, CA, say they may have found a way to trigger tissue repair in damaged muscles, which could help treat

Children’s Hospital Therapy Services Help Children With Muscular Dystrophy Gain Independence

University of Missouri Health System, by Staff ~ August 29, 2014 COLUMBIA, Mo. — Muscular dystrophy is a progressive disease that weakens muscles in the body. The condition can affect a wide range of everyday functions in children, anything from problems with just writing down a note to difficulty breathing. Specialists at University of Missouri

MU Researchers Find Gene Therapy Protects Mice from Heart Condition

University of Missouri Health System, by Staff ~ August 20, 2014 The condition is a leading cause of death for those with Duchenne muscular dystrophy A new gene therapy developed by researchers at the University of Missouri School of Medicine has shown to protect mice from a life-threatening heart condition caused by muscular dystrophy. “This

New gene editing method shows promising results for correcting muscular dystrophy

Medical XPress, Provided by UT Southwestern Medical Center ~ August 14, 2014 Researchers used a technique called CRISPR/Cas9-mediated genome editing, which can precisely remove a mutation in DNA, allowing the body's DNA repair mechanisms to replace it with a normal copy of the gene. The benefit of this over other gene therapy techniques is that

Discovery of a ‘conductor’ in muscle development could impact on the treatment of muscular diseases

ScienceDaily, by Staff ~ February 25, 2014 A team led by Jean-François Côté, researcher at the IRCM, identified a ''conductor'' in the development of muscle tissue. The discovery, published online by the scientific journal Proceedings of the National Academy of Sciences (PNAS), could have an important impact on the treatment of muscular diseases such as

Nanoparticles treat muscular dystrophy in mice

Washington University in St. Louis, by Julia Evangelou Strait ~ February 11, 2014 Researchers at Washington University School of Medicine in St. Louis have demonstrated a new approach to treating muscular dystrophy. Mice with a form of this muscle-weakening disease showed improved strength and heart function when treated with nanoparticles loaded with rapamycin, an immunosuppressive

Implantable ventilator device marks first licensing deal for Cleveland Clinic’s Innovation Alliance

MedCity News, by Deanna Pogorelc ~ December 2, 2013 A new licensing agreement with Maryland tech company InnoVital Systems marks an important milestone for the Cleveland Clinic’s commercialization arm as the first such deal to come out of the its seven-member Healthcare Innovation Alliance. InnoVital Systems, which develops sensors, robotics and electronics for the defense

Gene Therapy Helps Muscular Dystrophy Patients Breathe Easier

RegenerativeMedicine.net, by Staff ~ June 27, 2013 “This approach to treating an inherited disease that affects respiratory function has been safe and we are pleased to see it was also effective at reversing some of the respiratory deficits these patients had,” said Dr. Barry Byrne. Children with a rare form of muscular dystrophy called Pompe