Home/Tag: Gene

$3 million to help expand Wolfram syndrome research

Researchers at Washington University School of Medicine in St. Louis have received a five-year, $3 million grant to study Wolfram syndrome, a rare genetic disorder that causes neurologic problems, insulin-dependent diabetes and other serious conditions. The new grant, from the Eunice Kennedy Shriver National Institute of Child Health & Human Development of the National Institutes

November 20th, 2018|Categories: Around The State, Clinical Trials|Tags: , |

FDA Approves First Gene Therapy for non-Hodgkin Lymphoma

The U.S. Food and Drug Administration (FDA) approved axicabtagene ciloleucel (Yescarta) to treat adult patients with certain types of large B-cell lymphoma who have not responded to or who have relapsed after at least two other kinds of treatment. Kite Pharma’s Yescarta, a chimeric antigen receptor (CAR) T cell therapy, is the second gene therapy

October 28th, 2017|Categories: Cancer, Disease Specific|Tags: , , |

Alzheimer’s gene poses both risk — and benefits

Scientists drilling down to the molecular roots of Alzheimer’s disease have encountered a good news/bad news scenario. A major player is a gene called TREM2, mutations of which can substantially raise a person’s risk of the disease. The bad news is that in the early stages of the disease, high-risk TREM2 variants can hobble the

Gene Editing Spurs Hope for Transplanting Pig Organs Into Humans

In a striking advance that helps open the door to organ transplants from animals, researchers have created gene-edited piglets cleansed of viruses that might cause disease in humans. The experiments, reported on Thursday in the journal Science, may make it possible one day to transplant livers, hearts and other organs from pigs into humans, a

August 17th, 2017|Categories: General News|Tags: , , , |