First Gene Therapy for Tay-Sachs Disease Successfully Given to Two Children

First Gene Therapy for Tay-Sachs Disease Successfully Given to Two Children Two babies have received the first-ever gene therapy for Tay-Sachs disease after over 14 years of development. Tay-Sachs is a severe neurological disease caused by a deficiency in an enzyme called HexA. This enzyme breaks down a fatlike substance